NHS drugs go-ahead offers lifeline to children with rare muscle-wasting disease

Medicines watchdog approves two treatments for patients with spinal muscular atrophy Hundreds of children with a rare muscle-wasting disease will be able to receive two drugs that can improve their survival in a move parents hailed as a “lifeline”. The National Institute for Health and Care Excellence (Nice) has published final draft guidance recommending that any patient who would benefit can have either drug.